1 Report Overview 1.1 Study Scope 1.2 Market Analysis by Type 1.2.1 Global Hemophilia Gene Therapy Market Size Growth Rate by Type: 2017 VS 2021 VS 2028 1.2.2 Hemophilia A 1.2.3 Hemophilia B 1.3 Market by Application 1.3.1 Global Hemophilia Gene Therapy Market Share by Application: 2017 VS 2021 VS 2028 1.3.2 Hemophilia A Gene Therapy 1.3.3 Hemophilia B Gene Therapy 1.4 Study Objectives 1.5 Years Considered 2 Global Growth Trends 2.1 Global Hemophilia Gene Therapy Market Perspective (2017-2028) 2.2 Hemophilia Gene Therapy Growth Trends by Region 2.2.1 Hemophilia Gene Therapy Market Size by Region: 2017 VS 2021 VS 2028 2.2.2 Hemophilia Gene Therapy Historic Market Size by Region (2017-2022) 2.2.3 Hemophilia Gene Therapy Forecasted Market Size by Region (2023-2028) 2.3 Hemophilia Gene Therapy Market Dynamics 2.3.1 Hemophilia Gene Therapy Industry Trends 2.3.2 Hemophilia Gene Therapy Market Drivers 2.3.3 Hemophilia Gene Therapy Market Challenges 2.3.4 Hemophilia Gene Therapy Market Restraints 3 Competition Landscape by Key Players 3.1 Global Top Hemophilia Gene Therapy Players by Revenue 3.1.1 Global Top Hemophilia Gene Therapy Players by Revenue (2017-2022) 3.1.2 Global Hemophilia Gene Therapy Revenue Market Share by Players (2017-2022) 3.2 Global Hemophilia Gene Therapy Market Share by Company Type (Tier 1, Tier 2, and Tier 3) 3.3 Players Covered: Ranking by Hemophilia Gene Therapy Revenue 3.4 Global Hemophilia Gene Therapy Market Concentration Ratio 3.4.1 Global Hemophilia Gene Therapy Market Concentration Ratio (CR5 and HHI) 3.4.2 Global Top 10 and Top 5 Companies by Hemophilia Gene Therapy Revenue in 2021 3.5 Hemophilia Gene Therapy Key Players Head office and Area Served 3.6 Key Players Hemophilia Gene Therapy Product Solution and Service 3.7 Date of Enter into Hemophilia Gene Therapy Market 3.8 Mergers & Acquisitions, Expansion Plans 4 Hemophilia Gene Therapy Breakdown Data by Type 4.1 Global Hemophilia Gene Therapy Historic Market Size by Type (2017-2022) 4.2 Global Hemophilia Gene Therapy Forecasted Market Size by Type (2023-2028) 5 Hemophilia Gene Therapy Breakdown Data by Application 5.1 Global Hemophilia Gene Therapy Historic Market Size by Application (2017-2022) 5.2 Global Hemophilia Gene Therapy Forecasted Market Size by Application (2023-2028) 6 North America 6.1 North America Hemophilia Gene Therapy Market Size (2017-2028) 6.2 North America Hemophilia Gene Therapy Market Size by Country (2017-2022) 6.3 North America Hemophilia Gene Therapy Market Size by Country (2023-2028) 6.4 United States 6.5 Canada 7 Europe 7.1 Europe Hemophilia Gene Therapy Market Size (2017-2028) 7.2 Europe Hemophilia Gene Therapy Market Size by Country (2017-2022) 7.3 Europe Hemophilia Gene Therapy Market Size by Country (2023-2028) 7.4 Germany 7.5 France 7.6 U.K. 7.7 Italy 7.8 Russia 7.9 Nordic Countries 8 Asia-Pacific 8.1 Asia-Pacific Hemophilia Gene Therapy Market Size (2017-2028) 8.2 Asia-Pacific Hemophilia Gene Therapy Market Size by Country (2017-2022) 8.3 Asia-Pacific Hemophilia Gene Therapy Market Size by Country (2023-2028) 8.4 China 8.5 Japan 8.6 South Korea 8.7 Southeast Asia 8.8 India 8.9 Australia 9 Latin America 9.1 Latin America Hemophilia Gene Therapy Market Size (2017-2028) 9.2 Latin America Hemophilia Gene Therapy Market Size by Country (2017-2022) 9.3 Latin America Hemophilia Gene Therapy Market Size by Country (2023-2028) 9.4 Mexico 9.5 Brazil 10 Middle East & Africa 10.1 Middle East & Africa Hemophilia Gene Therapy Market Size (2017-2028) 10.2 Middle East & Africa Hemophilia Gene Therapy Market Size by Country (2017-2022) 10.3 Middle East & Africa Hemophilia Gene Therapy Market Size by Country (2023-2028) 10.4 Turkey 10.5 Saudi Arabia 10.6 UAE 11 Key Players Profiles 11.1 Spark Therapeutics 11.1.1 Spark Therapeutics Company Detail 11.1.2 Spark Therapeutics Business Overview 11.1.3 Spark Therapeutics Hemophilia Gene Therapy Introduction 11.1.4 Spark Therapeutics Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.1.5 Spark Therapeutics Recent Development 11.2 Ultragenyx 11.2.1 Ultragenyx Company Detail 11.2.2 Ultragenyx Business Overview 11.2.3 Ultragenyx Hemophilia Gene Therapy Introduction 11.2.4 Ultragenyx Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.2.5 Ultragenyx Recent Development 11.3 Shire PLC 11.3.1 Shire PLC Company Detail 11.3.2 Shire PLC Business Overview 11.3.3 Shire PLC Hemophilia Gene Therapy Introduction 11.3.4 Shire PLC Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.3.5 Shire PLC Recent Development 11.4 Sangamo Therapeutics 11.4.1 Sangamo Therapeutics Company Detail 11.4.2 Sangamo Therapeutics Business Overview 11.4.3 Sangamo Therapeutics Hemophilia Gene Therapy Introduction 11.4.4 Sangamo Therapeutics Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.4.5 Sangamo Therapeutics Recent Development 11.5 Bioverativ 11.5.1 Bioverativ Company Detail 11.5.2 Bioverativ Business Overview 11.5.3 Bioverativ Hemophilia Gene Therapy Introduction 11.5.4 Bioverativ Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.5.5 Bioverativ Recent Development 11.6 BioMarin 11.6.1 BioMarin Company Detail 11.6.2 BioMarin Business Overview 11.6.3 BioMarin Hemophilia Gene Therapy Introduction 11.6.4 BioMarin Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.6.5 BioMarin Recent Development 11.7 uniQure 11.7.1 uniQure Company Detail 11.7.2 uniQure Business Overview 11.7.3 uniQure Hemophilia Gene Therapy Introduction 11.7.4 uniQure Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.7.5 uniQure Recent Development 11.8 Freeline Therapeutics 11.8.1 Freeline Therapeutics Company Detail 11.8.2 Freeline Therapeutics Business Overview 11.8.3 Freeline Therapeutics Hemophilia Gene Therapy Introduction 11.8.4 Freeline Therapeutics Revenue in Hemophilia Gene Therapy Business (2017-2022) 11.8.5 Freeline Therapeutics Recent Development 12 Analyst's Viewpoints/Conclusions 13 Appendix 13.1 Research Methodology 13.1.1 Methodology/Research Approach 13.1.2 Data Source 13.2 Disclaimer 13.3 Author Details

List of Tables Table 1. Global Hemophilia Gene Therapy Market Size Growth Rate by Type (US$ Million): 2017 VS 2021 VS 2028 Table 2. Key Players of Hemophilia A Table 3. Key Players of Hemophilia B Table 4. Global Hemophilia Gene Therapy Market Size Growth by Application (US$ Million): 2017 VS 2021 VS 2028 Table 5. Global Hemophilia Gene Therapy Market Size by Region (US$ Million): 2017 VS 2021 VS 2028 Table 6. Global Hemophilia Gene Therapy Market Size by Region (2017-2022) & (US$ Million) Table 7. Global Hemophilia Gene Therapy Market Share by Region (2017-2022) Table 8. Global Hemophilia Gene Therapy Forecasted Market Size by Region (2023-2028) & (US$ Million) Table 9. Global Hemophilia Gene Therapy Market Share by Region (2023-2028) Table 10. Hemophilia Gene Therapy Market Trends Table 11. Hemophilia Gene Therapy Market Drivers Table 12. Hemophilia Gene Therapy Market Challenges Table 13. Hemophilia Gene Therapy Market Restraints Table 14. Global Hemophilia Gene Therapy Revenue by Players (2017-2022) & (US$ Million) Table 15. Global Hemophilia Gene Therapy Market Share by Players (2017-2022) Table 16. Global Top Hemophilia Gene Therapy Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Hemophilia Gene Therapy as of 2021) Table 17. Ranking of Global Top Hemophilia Gene Therapy Companies by Revenue (US$ Million) in 2021 Table 18. Global 5 Largest Players Market Share by Hemophilia Gene Therapy Revenue (CR5 and HHI) & (2017-2022) Table 19. Key Players Headquarters and Area Served Table 20. Key Players Hemophilia Gene Therapy Product Solution and Service Table 21. Date of Enter into Hemophilia Gene Therapy Market Table 22. Mergers & Acquisitions, Expansion Plans Table 23. Global Hemophilia Gene Therapy Market Size by Type (2017-2022) & (US$ Million) Table 24. Global Hemophilia Gene Therapy Revenue Market Share by Type (2017-2022) Table 25. Global Hemophilia Gene Therapy Forecasted Market Size by Type (2023-2028) & (US$ Million) Table 26. Global Hemophilia Gene Therapy Revenue Market Share by Type (2023-2028) Table 27. Global Hemophilia Gene Therapy Market Size by Application (2017-2022) & (US$ Million) Table 28. Global Hemophilia Gene Therapy Revenue Market Share by Application (2017-2022) Table 29. Global Hemophilia Gene Therapy Forecasted Market Size by Application (2023-2028) & (US$ Million) Table 30. Global Hemophilia Gene Therapy Revenue Market Share by Application (2023-2028) Table 31. North America Hemophilia Gene Therapy Market Size by Country (2017-2022) & (US$ Million) Table 32. North America Hemophilia Gene Therapy Market Size by Country (2023-2028) & (US$ Million) Table 33. Europe Hemophilia Gene Therapy Market Size by Country (2017-2022) & (US$ Million) Table 34. Europe Hemophilia Gene Therapy Market Size by Country (2023-2028) & (US$ Million) Table 35. Asia-Pacific Hemophilia Gene Therapy Market Size by Region (2017-2022) & (US$ Million) Table 36. Asia-Pacific Hemophilia Gene Therapy Market Size by Region (2023-2028) & (US$ Million) Table 37. Latin America Hemophilia Gene Therapy Market Size by Country (2017-2022) & (US$ Million) Table 38. Latin America Hemophilia Gene Therapy Market Size by Country (2023-2028) & (US$ Million) Table 39. Middle East & Africa Hemophilia Gene Therapy Market Size by Country (2017-2022) & (US$ Million) Table 40. Middle East & Africa Hemophilia Gene Therapy Market Size by Country (2023-2028) & (US$ Million) Table 41. Spark Therapeutics Company Detail Table 42. Spark Therapeutics Business Overview Table 43. Spark Therapeutics Hemophilia Gene Therapy Product Table 44. Spark Therapeutics Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 45. Spark Therapeutics Recent Development Table 46. Ultragenyx Company Detail Table 47. Ultragenyx Business Overview Table 48. Ultragenyx Hemophilia Gene Therapy Product Table 49. Ultragenyx Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 50. Ultragenyx Recent Development Table 51. Shire PLC Company Detail Table 52. Shire PLC Business Overview Table 53. Shire PLC Hemophilia Gene Therapy Product Table 54. Shire PLC Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 55. Shire PLC Recent Development Table 56. Sangamo Therapeutics Company Detail Table 57. Sangamo Therapeutics Business Overview Table 58. Sangamo Therapeutics Hemophilia Gene Therapy Product Table 59. Sangamo Therapeutics Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 60. Sangamo Therapeutics Recent Development Table 61. Bioverativ Company Detail Table 62. Bioverativ Business Overview Table 63. Bioverativ Hemophilia Gene Therapy Product Table 64. Bioverativ Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 65. Bioverativ Recent Development Table 66. BioMarin Company Detail Table 67. BioMarin Business Overview Table 68. BioMarin Hemophilia Gene Therapy Product Table 69. BioMarin Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 70. BioMarin Recent Development Table 71. uniQure Company Detail Table 72. uniQure Business Overview Table 73. uniQure Hemophilia Gene Therapy Product Table 74. uniQure Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 75. uniQure Recent Development Table 76. Freeline Therapeutics Company Detail Table 77. Freeline Therapeutics Business Overview Table 78. Freeline Therapeutics Hemophilia Gene Therapy Product Table 79. Freeline Therapeutics Revenue in Hemophilia Gene Therapy Business (2017-2022) & (US$ Million) Table 80. Freeline Therapeutics Recent Development Table 81. Research Programs/Design for This Report Table 82. Key Data Information from Secondary Sources Table 83. Key Data Information from Primary Sources List of Figures Figure 1. Global Hemophilia Gene Therapy Market Share by Type: 2021 VS 2028 Figure 2. Hemophilia A Features Figure 3. Hemophilia B Features Figure 4. Global Hemophilia Gene Therapy Market Share by Application in 2021 & 2028 Figure 5. Hemophilia A Gene Therapy Case Studies Figure 6. Hemophilia B Gene Therapy Case Studies Figure 7. Hemophilia Gene Therapy Report Years Considered Figure 8. Global Hemophilia Gene Therapy Market Size (US$ Million), Year-over-Year: 2017-2028 Figure 9. Global Hemophilia Gene Therapy Market Size, (US$ Million), 2017 VS 2021 VS 2028 Figure 10. Global Hemophilia Gene Therapy Market Share by Region: 2021 VS 2028 Figure 11. Global Hemophilia Gene Therapy Market Share by Players in 2021 Figure 12. Global Top Hemophilia Gene Therapy Players by Company Type (Tier 1, Tier 2, and Tier 3) & (based on the Revenue in Hemophilia Gene Therapy as of 2021) Figure 13. The Top 10 and 5 Players Market Share by Hemophilia Gene Therapy Revenue in 2021 Figure 14. North America Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 15. North America Hemophilia Gene Therapy Market Share by Country (2017-2028) Figure 16. United States Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 17. Canada Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 18. Europe Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 19. Europe Hemophilia Gene Therapy Market Share by Country (2017-2028) Figure 20. Germany Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 21. France Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 22. U.K. Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 23. Italy Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 24. Russia Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 25. Nordic Countries Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 26. Asia-Pacific Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 27. Asia-Pacific Hemophilia Gene Therapy Market Share by Region (2017-2028) Figure 28. China Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 29. Japan Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 30. South Korea Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 31. Southeast Asia Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 32. India Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 33. Australia Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 34. Latin America Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 35. Latin America Hemophilia Gene Therapy Market Share by Country (2017-2028) Figure 36. Mexico Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 37. Brazil Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 38. Middle East & Africa Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 39. Middle East & Africa Hemophilia Gene Therapy Market Share by Country (2017-2028) Figure 40. Turkey Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 41. Saudi Arabia Hemophilia Gene Therapy Market Size YoY Growth (2017-2028) & (US$ Million) Figure 42. Spark Therapeutics Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 43. Ultragenyx Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 44. Shire PLC Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 45. Sangamo Therapeutics Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 46. Bioverativ Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 47. BioMarin Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 48. uniQure Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 49. Freeline Therapeutics Revenue Growth Rate in Hemophilia Gene Therapy Business (2017-2022) Figure 50. Bottom-up and Top-down Approaches for This Report Figure 51. Data Triangulation Figure 52. Key Executives Interviewed

Spark Therapeutics Ultragenyx Shire PLC Sangamo Therapeutics Bioverativ BioMarin uniQure Freeline Therapeutics